No abstract available
MeSH terms
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Cerebroside-Sulfatase / genetics*
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Genetic Therapy / methods*
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Hematopoietic Stem Cell Transplantation*
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Hematopoietic Stem Cells / metabolism*
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Humans
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Leukodystrophy, Metachromatic / therapy*
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Male
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Wiskott-Aldrich Syndrome / therapy*
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Wiskott-Aldrich Syndrome Protein / genetics*
Substances
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Wiskott-Aldrich Syndrome Protein
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Cerebroside-Sulfatase