No abstract available
MeSH terms
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Clinical Trials as Topic
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Genetic Therapy
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Humans
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Male
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Muscular Dystrophy, Duchenne / drug therapy*
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Muscular Dystrophy, Duchenne / genetics*
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Oligonucleotides / therapeutic use*
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Utrophin / genetics*
Substances
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Oligonucleotides
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PRO051
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Utrophin