To skip or not to skip: that is the question for duchenne muscular dystrophy

Mol Ther. 2013 Dec;21(12):2131-2. doi: 10.1038/mt.2013.252.
No abstract available

Publication types

  • Editorial

MeSH terms

  • Clinical Trials as Topic
  • Genetic Therapy
  • Humans
  • Male
  • Muscular Dystrophy, Duchenne / drug therapy*
  • Muscular Dystrophy, Duchenne / genetics*
  • Oligonucleotides / therapeutic use*
  • Utrophin / genetics*

Substances

  • Oligonucleotides
  • PRO051
  • Utrophin