CRISPR therapy shows promise in Duchenne muscular dystrophy

Nat Rev Neurol. 2018 Nov;14(11):632-633. doi: 10.1038/s41582-018-0078-8.
No abstract available

Publication types

  • Comment

MeSH terms

  • Animals
  • CRISPR-Cas Systems
  • Clustered Regularly Interspaced Short Palindromic Repeats
  • Dogs
  • Dystrophin*
  • Gene Editing
  • Muscular Dystrophy, Duchenne*

Substances

  • Dystrophin