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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2010 1
2011 1
2012 1
2013 4
2014 2
2015 4
2016 2
2017 3
2018 2
2021 2
2022 1
2023 1
2024 0

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21 results

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Page 1
Defective membrane fusion and repair in Anoctamin5-deficient muscular dystrophy.
Griffin DA, Johnson RW, Whitlock JM, Pozsgai ER, Heller KN, Grose WE, Arnold WD, Sahenk Z, Hartzell HC, Rodino-Klapac LR. Griffin DA, et al. Among authors: heller kn. Hum Mol Genet. 2016 May 15;25(10):1900-1911. doi: 10.1093/hmg/ddw063. Epub 2016 Feb 23. Hum Mol Genet. 2016. PMID: 26911675 Free PMC article.
AAV.Dysferlin Overlap Vectors Restore Function in Dysferlinopathy Animal Models.
Sondergaard PC, Griffin DA, Pozsgai ER, Johnson RW, Grose WE, Heller KN, Shontz KM, Montgomery CL, Liu J, Clark KR, Sahenk Z, Mendell JR, Rodino-Klapac LR. Sondergaard PC, et al. Among authors: heller kn. Ann Clin Transl Neurol. 2015 Mar;2(3):256-70. doi: 10.1002/acn3.172. Epub 2015 Jan 20. Ann Clin Transl Neurol. 2015. PMID: 25815352 Free PMC article.
AAV-mediated follistatin gene therapy improves functional outcomes in the TIC-DUX4 mouse model of FSHD.
Giesige CR, Wallace LM, Heller KN, Eidahl JO, Saad NY, Fowler AM, Pyne NK, Al-Kharsan M, Rashnonejad A, Chermahini GA, Domire JS, Mukweyi D, Garwick-Coppens SE, Guckes SM, McLaughlin KJ, Meyer K, Rodino-Klapac LR, Harper SQ. Giesige CR, et al. Among authors: heller kn. JCI Insight. 2018 Nov 15;3(22):e123538. doi: 10.1172/jci.insight.123538. JCI Insight. 2018. PMID: 30429376 Free PMC article.
Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy.
Potter RA, Griffin DA, Sondergaard PC, Johnson RW, Pozsgai ER, Heller KN, Peterson EL, Lehtimäki KK, Windish HP, Mittal PJ, Albrecht DE, Mendell JR, Rodino-Klapac LR. Potter RA, et al. Among authors: heller kn. Hum Gene Ther. 2018 Jul;29(7):749-762. doi: 10.1089/hum.2017.062. Epub 2017 Jul 13. Hum Gene Ther. 2018. PMID: 28707952 Free PMC article.
Micro-dystrophin and follistatin co-delivery restores muscle function in aged DMD model.
Rodino-Klapac LR, Janssen PM, Shontz KM, Canan B, Montgomery CL, Griffin D, Heller K, Schmelzer L, Handy C, Clark KR, Sahenk Z, Mendell JR, Kaspar BK. Rodino-Klapac LR, et al. Among authors: heller k. Hum Mol Genet. 2013 Dec 15;22(24):4929-37. doi: 10.1093/hmg/ddt342. Epub 2013 Jul 17. Hum Mol Genet. 2013. PMID: 23863459 Free PMC article.
21 results