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Table representation of search results timeline featuring number of search results per year.

Year Number of Results
2002 1
2003 2
2004 2
2006 1
2007 1
2009 1
2010 2
2011 1
2012 3
2013 2
2014 3
2015 2
2017 2
2019 2
2021 1
2023 4
2024 1

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29 results

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Page 1
Identification of Safe and Effective Intravenous Dose of AAVrh.10hFXN to Treat the Cardiac Manifestations of Friedreich's Ataxia.
Munoz-Zuluaga C, Gertz M, Yost-Bido M, Greco A, Gorman N, Chen A, Kooner V, Rosenberg JB, De BP, Kaminsky SM, Borczuk A, Ricart Arbona RJ, Martin HR, Monette S, Khanna R, Barth JA, Crystal RG, Sondhi D. Munoz-Zuluaga C, et al. Among authors: khanna r. Hum Gene Ther. 2023 Jul;34(13-14):605-615. doi: 10.1089/hum.2023.020. Epub 2023 Jul 4. Hum Gene Ther. 2023. PMID: 37166361
Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease.
De BP, Rosenberg JB, Selvan N, Wilson I, Yusufzai N, Greco A, Kaminsky SM, Heier LA, Ricart Arbona RJ, Miranda IC, Monette S, Nair A, Khanna R, Crystal RG, Sondhi D. De BP, et al. Among authors: khanna r. Hum Gene Ther. 2023 Sep;34(17-18):905-916. doi: 10.1089/hum.2023.067. Hum Gene Ther. 2023. PMID: 37624739
Improved efficacy of a next-generation ERT in murine Pompe disease.
Xu S, Lun Y, Frascella M, Garcia A, Soska R, Nair A, Ponery AS, Schilling A, Feng J, Tuske S, Valle MCD, Martina JA, Ralston E, Gotschall R, Valenzano KJ, Puertollano R, Do HV, Raben N, Khanna R. Xu S, et al. Among authors: khanna r. JCI Insight. 2019 Mar 7;4(5):e125358. doi: 10.1172/jci.insight.125358. eCollection 2019 Mar 7. JCI Insight. 2019. PMID: 30843882 Free PMC article.
Expression and processing of mature human frataxin after gene therapy in mice.
Rojsajjakul T, Selvan N, De B, Rosenberg JB, Kaminsky SM, Sondhi D, Janki P, Crystal RG, Mesaros C, Khanna R, Blair IA. Rojsajjakul T, et al. Among authors: khanna r. Res Sq [Preprint]. 2023 Dec 28:rs.3.rs-3788652. doi: 10.21203/rs.3.rs-3788652/v1. Res Sq. 2023. PMID: 38234818 Free PMC article. Updated. Preprint.
Activation of transglutaminase in mu-calpain null erythrocytes.
O'Neill GM, Prasanna Murthy SN, Lorand L, Khanna R, Liu SC, Hanspal M, Hanada T, Chishti AH. O'Neill GM, et al. Among authors: khanna r. Biochem Biophys Res Commun. 2003 Jul 25;307(2):327-31. doi: 10.1016/s0006-291x(03)01184-7. Biochem Biophys Res Commun. 2003. PMID: 12859959
Migalastat Tissue Distribution: Extrapolation From Mice to Humans Using Pharmacokinetic Modeling and Comparison With Agalsidase Beta Tissue Distribution in Mice.
Wu YS, Khanna R, Schmith V, Lun Y, Shen JS, Garcia A, Dungan L, Perry A, Martin L, Tsai PC, Hamler R, Das AM, Schiffmann R, Johnson FK. Wu YS, et al. Among authors: khanna r. Clin Pharmacol Drug Dev. 2021 Sep;10(9):1075-1088. doi: 10.1002/cpdd.941. Epub 2021 Apr 19. Clin Pharmacol Drug Dev. 2021. PMID: 33876577 Free PMC article.
29 results