Mutant allele knockout with novel CRISPR nuclease promotes myelopoiesis in ELANE neutropenia.
Sabo P, Makaryan V, Dicken Y, Povodovski L, Rockah L, Bar T, Gabay M, Elinger D, Segal E, Haimov O, Antoshvili M, Drori AL, Poulsen T, Herman A, Emmanuel R, Dale DC.
Sabo P, et al. Among authors: drori al.
Mol Ther Methods Clin Dev. 2022 Jun 9;26:119-131. doi: 10.1016/j.omtm.2022.06.002. eCollection 2022 Sep 8.
Mol Ther Methods Clin Dev. 2022.
PMID: 35795780
Free PMC article.