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Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency.
N Engl J Med. 2021 May 27;384(21):2002-2013. doi: 10.1056/NEJMoa2027675. Epub 2021 May 11.
N Engl J Med. 2021.
PMID: 33974366
Free PMC article.
Clinical Trial.
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency.
Reinhardt B, Habib O, Shaw KL, Garabedian E, Carbonaro-Sarracino DA, Terrazas D, Fernandez BC, De Oliveira S, Moore TB, Ikeda AK, Engel BC, Podsakoff GM, Hollis RP, Fernandes A, Jackson C, Shupien S, Mishra S, Davila A, Mottahedeh J, Vitomirov A, Meng W, Rosenfeld AM, Roche AM, Hokama P, Reddy S, Everett J, Wang X, Luning Prak ET, Cornetta K, Hershfield MS, Sokolic R, De Ravin SS, Malech HL, Bushman FD, Candotti F, Kohn DB.
Reinhardt B, et al. Among authors: terrazas d.
Blood. 2021 Oct 14;138(15):1304-1316. doi: 10.1182/blood.2020010260.
Blood. 2021.
PMID: 33974038
Free PMC article.
Clinical Trial.
Item in Clipboard
Lentiviral gene therapy for X-linked chronic granulomatous disease.
Kohn DB, Booth C, Kang EM, Pai SY, Shaw KL, Santilli G, Armant M, Buckland KF, Choi U, De Ravin SS, Dorsey MJ, Kuo CY, Leon-Rico D, Rivat C, Izotova N, Gilmour K, Snell K, Dip JX, Darwish J, Morris EC, Terrazas D, Wang LD, Bauser CA, Paprotka T, Kuhns DB, Gregg J, Raymond HE, Everett JK, Honnet G, Biasco L, Newburger PE, Bushman FD, Grez M, Gaspar HB, Williams DA, Malech HL, Galy A, Thrasher AJ; Net4CGD consortium.
Kohn DB, et al. Among authors: terrazas d.
Nat Med. 2020 Feb;26(2):200-206. doi: 10.1038/s41591-019-0735-5. Epub 2020 Jan 27.
Nat Med. 2020.
PMID: 31988463
Free PMC article.
Clinical Trial.
Item in Clipboard
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.
Shaw KL, Garabedian E, Mishra S, Barman P, Davila A, Carbonaro D, Shupien S, Silvin C, Geiger S, Nowicki B, Smogorzewska EM, Brown B, Wang X, de Oliveira S, Choi Y, Ikeda A, Terrazas D, Fu PY, Yu A, Fernandez BC, Cooper AR, Engel B, Podsakoff G, Balamurugan A, Anderson S, Muul L, Jagadeesh GJ, Kapoor N, Tse J, Moore TB, Purdy K, Rishi R, Mohan K, Skoda-Smith S, Buchbinder D, Abraham RS, Scharenberg A, Yang OO, Cornetta K, Gjertson D, Hershfield M, Sokolic R, Candotti F, Kohn DB.
Shaw KL, et al. Among authors: terrazas d.
J Clin Invest. 2017 May 1;127(5):1689-1699. doi: 10.1172/JCI90367. Epub 2017 Mar 27.
J Clin Invest. 2017.
PMID: 28346229
Free PMC article.
Clinical Trial.
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Findings on Optical Coherence Tomography in Malignant Infantile Osteopetrosis.
Campagna GA, Chew L, Pettenkofer M, Nicoletti E, Schwartz JD, Choi G, Fernandes AO, Terrazas D, Kohn DB, Tsui I.
Campagna GA, et al. Among authors: terrazas d.
Ophthalmic Surg Lasers Imaging Retina. 2022 Jul;53(7):398-402. doi: 10.3928/23258160-20220613-01. Epub 2022 Jul 1.
Ophthalmic Surg Lasers Imaging Retina. 2022.
PMID: 35858232
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Managing polymyalgia rheumatica and giant cell arteritis in the primary care setting.
Terrazas D, Schumann L.
Terrazas D, et al.
J Am Acad Nurse Pract. 1997 Jun;9(6):289-92, quiz 294-6. doi: 10.1111/j.1745-7599.1997.tb00723.x.
J Am Acad Nurse Pract. 1997.
PMID: 9274251
No abstract available.
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