Lentiviral Stem Cell Gene Therapy for Pompe Disease.
Liang Q, Stok M, van Helsdingen Y, van der Velden G, Jacobs E, Duncker D, Reuser A, van der Ploeg A, Vulto A, van Til NP, Wagemaker G.
Liang Q, et al. Among authors: jacobs e.
J Neuromuscul Dis. 2015;2(s1):S64.
J Neuromuscul Dis. 2015.
PMID: 27858653
No abstract available.