Efficacy of nusinersen in type 1, 2 and 3 spinal muscular atrophy: Real world data from Hungarian patients.
Szabó L, Gergely A, Jakus R, Fogarasi A, Grosz Z, Molnár MJ, Andor I, Schulcz O, Goschler Á, Medveczky E, Czövek D, Herczegfalvi Á.
Szabó L, et al. Among authors: grosz z.
Eur J Paediatr Neurol. 2020 Jul;27:37-42. doi: 10.1016/j.ejpn.2020.05.002. Epub 2020 May 14.
Eur J Paediatr Neurol. 2020.
PMID: 32456992
Free article.