Treatment of brain disease in the mucopolysaccharidoses.
Scarpa M, Orchard PJ, Schulz A, Dickson PI, Haskins ME, Escolar ML, Giugliani R.
Scarpa M, et al. Among authors: dickson pi.
Mol Genet Metab. 2017 Dec;122S:25-34. doi: 10.1016/j.ymgme.2017.10.007. Epub 2017 Oct 16.
Mol Genet Metab. 2017.
PMID: 29153844
Free article.
Review.