Monia BP - Search Results

1

Antisense oligonucleotide-mediated Dnm2 knockdown prevents and reverts myotubular myopathy in mice.

Tasfaout H, Buono S, Guo S, Kretz C, Messaddeq N, Booten S, Greenlee S, Monia BP, Cowling BS, Laporte J. Tasfaout H, et al. Among authors: monia bp. Nat Commun. 2017 Jun 7;8:15661. doi: 10.1038/ncomms15661. Nat Commun. 2017. PMID: 28589938 Free PMC article.

2

Reducing dynamin 2 (DNM2) rescues DNM2-related dominant centronuclear myopathy.

Buono S, Ross JA, Tasfaout H, Levy Y, Kretz C, Tayefeh L, Matson J, Guo S, Kessler P, Monia BP, Bitoun M, Ochala J, Laporte J, Cowling BS. Buono S, et al. Among authors: monia bp. Proc Natl Acad Sci U S A. 2018 Oct 23;115(43):11066-11071. doi: 10.1073/pnas.1808170115. Epub 2018 Oct 5. Proc Natl Acad Sci U S A. 2018. PMID: 30291191 Free PMC article.

3

Clinical development of an antisense therapy for the treatment of transthyretin-associated polyneuropathy.

Ackermann EJ, Guo S, Booten S, Alvarado L, Benson M, Hughes S, Monia BP. Ackermann EJ, et al. Among authors: monia bp. Amyloid. 2012 Jun;19 Suppl 1:43-4. doi: 10.3109/13506129.2012.673140. Epub 2012 Apr 12. Amyloid. 2012. PMID: 22494066

4

Knockdown of Z Mutant Alpha-1 Antitrypsin In Vivo Using Modified DNA Antisense Oligonucleotides.

Aghajan M, Guo S, Monia BP. Aghajan M, et al. Among authors: monia bp. Methods Mol Biol. 2017;1639:127-138. doi: 10.1007/978-1-4939-7163-3_12. Methods Mol Biol. 2017. PMID: 28752452

5

Reducing TMPRSS6 ameliorates hemochromatosis and β-thalassemia in mice.

Guo S, Casu C, Gardenghi S, Booten S, Aghajan M, Peralta R, Watt A, Freier S, Monia BP, Rivella S. Guo S, et al. Among authors: monia bp. J Clin Invest. 2013 Apr;123(4):1531-41. doi: 10.1172/JCI66969. Epub 2013 Mar 25. J Clin Invest. 2013. PMID: 23524968 Free PMC article.

6

Suppressing transthyretin production in mice, monkeys and humans using 2nd-Generation antisense oligonucleotides.

Ackermann EJ, Guo S, Benson MD, Booten S, Freier S, Hughes SG, Kim TW, Jesse Kwoh T, Matson J, Norris D, Yu R, Watt A, Monia BP. Ackermann EJ, et al. Among authors: monia bp. Amyloid. 2016 Sep;23(3):148-157. doi: 10.1080/13506129.2016.1191458. Epub 2016 Jun 29. Amyloid. 2016. PMID: 27355239 Clinical Trial.

7

Inhaled ENaC antisense oligonucleotide ameliorates cystic fibrosis-like lung disease in mice.

Crosby JR, Zhao C, Jiang C, Bai D, Katz M, Greenlee S, Kawabe H, McCaleb M, Rotin D, Guo S, Monia BP. Crosby JR, et al. Among authors: monia bp. J Cyst Fibros. 2017 Nov;16(6):671-680. doi: 10.1016/j.jcf.2017.05.003. Epub 2017 May 20. J Cyst Fibros. 2017. PMID: 28539224 Free article.

8

Antisense oligonucleotide targeting of mRNAs encoding ENaC subunits α, β, and γ improves cystic fibrosis-like disease in mice.

Zhao C, Crosby J, Lv T, Bai D, Monia BP, Guo S. Zhao C, et al. Among authors: monia bp. J Cyst Fibros. 2019 May;18(3):334-341. doi: 10.1016/j.jcf.2018.07.006. Epub 2018 Aug 10. J Cyst Fibros. 2019. PMID: 30100257 Free article.

9

Targeting Translation Termination Machinery with Antisense Oligonucleotides for Diseases Caused by Nonsense Mutations.

Huang L, Aghajan M, Quesenberry T, Low A, Murray SF, Monia BP, Guo S. Huang L, et al. Among authors: monia bp. Nucleic Acid Ther. 2019 Aug;29(4):175-186. doi: 10.1089/nat.2019.0779. Epub 2019 May 9. Nucleic Acid Ther. 2019. PMID: 31070517 Free PMC article.

10

Antisense oligonucleotide treatment ameliorates IFN-γ-induced proteinuria in APOL1-transgenic mice.

Aghajan M, Booten SL, Althage M, Hart CE, Ericsson A, Maxvall I, Ochaba J, Menschik-Lundin A, Hartleib J, Kuntz S, Gattis D, Ahlström C, Watt AT, Engelhardt JA, Monia BP, Magnone MC, Guo S. Aghajan M, et al. Among authors: monia bp. JCI Insight. 2019 Jun 20;4(12):e126124. doi: 10.1172/jci.insight.126124. eCollection 2019 Jun 20. JCI Insight. 2019. PMID: 31217349 Free PMC article.

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