Toward responsible clinical n-of-1 strategies for rare diseases.
Defelippe VM, J M W van Thiel G, Otte WM, Schutgens REG, Stunnenberg B, Cross HJ, O'Callaghan F, De Giorgis V, Jansen FE, Perucca E, Brilstra EH, Braun KPJ.
Defelippe VM, et al. Among authors: otte wm.
Drug Discov Today. 2023 Oct;28(10):103688. doi: 10.1016/j.drudis.2023.103688. Epub 2023 Jun 24.
Drug Discov Today. 2023.
PMID: 37356616
Free article.
Review.