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iMyoblasts for ex vivo and in vivo investigations of human myogenesis and disease modeling.
Elife. 2022 Jan 25;11:e70341. doi: 10.7554/eLife.70341.
Elife. 2022.
PMID: 35076017
Free PMC article.
Endogenous DUX4 expression in FSHD myotubes is sufficient to cause cell death and disrupts RNA splicing and cell migration pathways.
Rickard AM, Petek LM, Miller DG.
Rickard AM, et al.
Hum Mol Genet. 2015 Oct 15;24(20):5901-14. doi: 10.1093/hmg/ddv315. Epub 2015 Aug 5.
Hum Mol Genet. 2015.
PMID: 26246499
Free PMC article.
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A non-viral genome editing platform for site-specific insertion of large transgenes.
Chaudhari N, Rickard AM, Roy S, Dröge P, Makhija H.
Chaudhari N, et al. Among authors: rickard am.
Stem Cell Res Ther. 2020 Sep 3;11(1):380. doi: 10.1186/s13287-020-01890-6.
Stem Cell Res Ther. 2020.
PMID: 32883366
Free PMC article.
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A cross sectional study of two independent cohorts identifies serum biomarkers for facioscapulohumeral muscular dystrophy (FSHD).
Petek LM, Rickard AM, Budech C, Poliachik SL, Shaw D, Ferguson MR, Tawil R, Friedman SD, Miller DG.
Petek LM, et al. Among authors: rickard am.
Neuromuscul Disord. 2016 Jul;26(7):405-13. doi: 10.1016/j.nmd.2016.04.012. Epub 2016 Apr 22.
Neuromuscul Disord. 2016.
PMID: 27185459
Free PMC article.
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