Prospects for gene therapy in cystic fibrosis

Arch Dis Child. 1999 Mar;80(3):286-9. doi: 10.1136/adc.80.3.286.
No abstract available

Publication types

  • Review

MeSH terms

  • Adolescent
  • Adult
  • Child
  • Child, Preschool
  • Costs and Cost Analysis
  • Cystic Fibrosis / genetics
  • Cystic Fibrosis / therapy*
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics
  • Cystic Fibrosis Transmembrane Conductance Regulator / physiology
  • Ethics, Medical
  • Genetic Therapy / economics
  • Genetic Therapy / methods*
  • Genetic Vectors
  • Humans
  • Infant
  • Infant, Newborn
  • Lung / metabolism

Substances

  • CFTR protein, human
  • Cystic Fibrosis Transmembrane Conductance Regulator