Variegated aneuploidy related to premature centromere division (PCD) is expressed in vivo and is a cancer-prone disease

Am J Med Genet. 2001 Jan 22;98(3):216-23. doi: 10.1002/1096-8628(20010122)98:3<216::aid-ajmg1091>3.0.co;2-0.

Abstract

We present three patients with variegated aneuploidy and premature centromere division (PCD), a rare chromosomal abnormality in humans. Comparison of these three and eight other patients with variegated aneuploidy related to PCD demonstrates a phenotype comprising most frequently microcephaly, CNS anomalies (with cerebellar affection and migration defects), mental retardation, pre-and postnatal growth retardation, flat and broad nasal bridge, apparently low-set ears, eye and skin abnormalities, and ambiguous genitalia in male patients. The occurrence of Wilms tumor in three patients, rhabdomyosarcoma in two others and acute leukemia in a fifth characterizes this condition as a chromosome or genome instability disorder with a high risk of malignancy. FISH studies in uncultured blood and buccal smear cells demonstrate that the random aneuploidies are not limited to cultured cells, but also occur in vivo.

Publication types

  • Case Reports
  • Review

MeSH terms

  • Abnormalities, Multiple / genetics
  • Abnormalities, Multiple / pathology
  • Adult
  • Aneuploidy*
  • Centromere / genetics*
  • Child
  • Cytogenetic Analysis
  • Female
  • Genetic Predisposition to Disease
  • Humans
  • Infant
  • Intellectual Disability / complications
  • Intellectual Disability / genetics
  • Male
  • Microcephaly / complications
  • Microcephaly / genetics
  • Neoplasms / etiology
  • Neoplasms / genetics*