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, 108 (1), 5-8

Muscular Dystrophy--Reason for Optimism?


Muscular Dystrophy--Reason for Optimism?

Edward A Burton et al. Cell.


Characterization of the mechanisms underlying various types of muscular dystrophy has been an outstanding triumph of molecular biology. Increasing clarification of the aberrant cellular processes responsible for these conditions may ultimately permit the development of effective means for molecular intervention, allowing correction of the abnormal cellular physiology that results in the dystrophic phenotype.

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