Low-molecular-weight polyethylenimine as a non-viral vector for DNA delivery: comparison of physicochemical properties, transfection efficiency and in vivo distribution with high-molecular-weight polyethylenimine

J Control Release. 2003 Apr 14;89(1):113-25. doi: 10.1016/s0168-3659(03)00076-2.

Abstract

Low-molecular-weight polyethylenimine (LMW-PEI) was synthesized by the acid-catalyzed, ring-opening polymerization of aziridine and compared with commercially available high-molecular-weight PEI (HMW-PEI) of 25 kDa. Molecular weights were determined by size-exclusion chromatography in combination with multi-angle laser light scattering. The weight average molecular weight (M(w)) of synthesized LMW-PEI was determined as 5.4+/-0.5 kDa, whereas commercial HMW-PEI showed a M(w) of 48+/-2 kDa. DNA polyplexes of LMW-PEI and HMW-PEI were characterized with regard to DNA condensation (ethidium bromide fluorescence quenching), size (photon correlation spectroscopy) and surface charge (laser Doppler anemometry). Compared with HMW-PEI, DNA condensation of LMW-PEI was slightly impaired at lower N/P ratios. Complexes with plasmid DNA at a N/P ratio of 6.7 showed significantly increased hydrodynamic diameters (590+/-140 vs. 160+/-10 nm), while the zeta-potential measurements were similar (23+/-2 vs. 30+/-3 mV). The cytotoxicity of LMW-PEI in L929 fibroblasts was reduced by more than one order of magnitude compared with HMW-PEI, as shown by MTT assay. LMW-PEI exhibited increased transfection efficiency in six different cell lines. Reporter gene expression was found to be increased by a factor of 2.1-110. The pharmacokinetics and biodistribution of 125I-PEI in mice were similar for both molecular weights with an AUC of ca. 330+/-100% ID/ml min. Approximately half of the injected dose accumulated in the liver. LMW-PEI proved to be an efficient gene delivery system in a broad range of cell lines. Due to differences in polyplex structure, as well as its relatively low cytotoxicity, which makes the application of high N/P ratios possible, LMW-PEI appears to possess advantageous qualities with regard to transfection efficiency over PEI of higher molecular weight.

MeSH terms

  • Action Potentials
  • Animals
  • Blood Chemical Analysis
  • Cell Line
  • Cricetinae
  • DNA / genetics*
  • DNA / metabolism*
  • Fibroblasts / drug effects
  • Gene Transfer Techniques*
  • Genes, Reporter / genetics*
  • Genetic Vectors / chemical synthesis*
  • Genetic Vectors / genetics*
  • Humans
  • In Vitro Techniques
  • Iodine Radioisotopes / blood
  • Iodine Radioisotopes / pharmacokinetics
  • Iodine Radioisotopes / urine
  • Kidney / drug effects
  • Kidney / metabolism
  • Liver / drug effects
  • Liver / metabolism
  • Lung / drug effects
  • Lung / metabolism
  • Mice
  • Molecular Weight*
  • Polyethyleneimine / chemical synthesis*
  • Polyethyleneimine / metabolism*
  • Polyethyleneimine / pharmacokinetics
  • Polyethyleneimine / toxicity*
  • Spleen / drug effects
  • Spleen / metabolism
  • Urinalysis

Substances

  • Iodine Radioisotopes
  • Polyethyleneimine
  • DNA