Two steps closer to gene therapy for cystic fibrosis

Nat Genet. 1992 Sep;2(1):4-5. doi: 10.1038/ng0992-4.
No abstract available

Publication types

  • News

MeSH terms

  • Animals
  • Cystic Fibrosis / genetics
  • Cystic Fibrosis / therapy*
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • Gene Expression
  • Genetic Therapy / trends*
  • Humans
  • Membrane Proteins / genetics
  • Mice
  • Mice, Transgenic

Substances

  • CFTR protein, human
  • Membrane Proteins
  • Cystic Fibrosis Transmembrane Conductance Regulator