Progress and prospects: gene therapy clinical trials (part 2)

Gene Ther. 2007 Nov;14(22):1555-63. doi: 10.1038/


This is the second part of a review summarizing progress and prospects in gene therapy clinical research. Twenty key diseases/strategies are succinctly described and commented on by leaders in the field. This part includes clinical trials for skin diseases, neurological disorders, HIV/AIDS, ornithine transcarbamylase deficiency, alpha(1)-antitrypsin deficiency, haemophilia and cancer.

Publication types

  • Review

MeSH terms

  • Clinical Trials as Topic
  • Gene Transfer Techniques / adverse effects
  • Gene Transfer Techniques / trends
  • Genetic Therapy / methods
  • Genetic Therapy / trends*
  • Genetic Vectors
  • Humans
  • Neoplasms / therapy
  • Stem Cell Transplantation / adverse effects
  • Stem Cell Transplantation / trends