Three-dimensional reconstruction of human cystic fibrosis transmembrane conductance regulator chloride channel revealed an ellipsoidal structure with orifices beneath the putative transmembrane domain

J Biol Chem. 2008 Oct 31;283(44):30300-10. doi: 10.1074/jbc.M803185200. Epub 2008 Aug 22.

Abstract

The cystic fibrosis transmembrane conductance regulator (CFTR) chloride channel is a membrane-integral protein that belongs to an ATP-binding cassette superfamily. Mutations in the CFTR gene cause cystic fibrosis in which salt, water, and protein transports are defective in various tissues. Here we expressed wild-type human CFTR as a FLAG-fused protein in HEK293 cells heterologously and purified it in three steps: anti-FLAG and wheat germ agglutinin affinity chromatographies and size exclusion chromatography. The stoichiometry of the protein was analyzed using various biochemical approaches, including chemical cross-linking, blue-native PAGE, size exclusion chromatography, and electron microscopy (EM) observation of antibody-decorated CFTR. All these data support a dimeric assembly of CFTR. Using 5,039 automatically selected particles from negatively stained EM images, the three-dimensional structure of CFTR was reconstructed at 2-nm resolution assuming a 2-fold symmetry. CFTR, presumably in a closed state, was shown to be an ellipsoidal particle with dimensions of 120 x 106 x 162 A. It comprises a small dome-shaped extracellular and membrane-spanning domain and a large cytoplasmic domain with orifices beneath the putative transmembrane domain. EM observation of CFTR.anti-regulatory domain antibody complex confirmed that two regulatory domains are located around the bottom end of the larger oval cytoplasmic domain.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cell Line
  • Cell Membrane / metabolism
  • Chromatography / methods
  • Cross-Linking Reagents / pharmacology
  • Cystic Fibrosis Transmembrane Conductance Regulator / metabolism*
  • Cytoplasm / metabolism
  • DNA, Complementary / metabolism
  • Gene Expression Regulation
  • Humans
  • Image Processing, Computer-Assisted
  • Kinetics
  • Microscopy, Electron, Transmission
  • Protein Binding
  • Protein Conformation
  • Protein Structure, Tertiary

Substances

  • Cross-Linking Reagents
  • DNA, Complementary
  • Cystic Fibrosis Transmembrane Conductance Regulator