Development of cellular immune responses against PAX5, a novel target for cancer immunotherapy

Cancer Res. 2008 Oct 1;68(19):8058-65. doi: 10.1158/0008-5472.CAN-08-0153.

Abstract

PAX5 is a member of the PAX family of developmental transcription factors with an important role in B-cell development. Its expression in normal adult tissue is limited to the hemopoietic system, but it is aberrantly expressed in a number of solid cancers and leukemias where it functions as an oncogene. We therefore hypothesized that anti-PAX5 immune responses could be used to target a number of malignancies without significant toxicity. We screened PAX5 peptides for the ability to bind HLA-A2 and identified a novel sequence, TLPGYPPHV (referred to as TLP). CTL lines against TLP were generated from peripheral blood of five normal HLA-A2-positive blood donors and showed specific HLA-A2-restricted killing against PAX5-expressing target cells. We generated high-avidity CTL clones from these lines capable of killing cells pulsed with <1 nmol/L of TLP and killing a range of PAX5-expressing malignant cell lines. I.v. injection of an anti-PAX5 CTL clone into immunodeficient mice bearing s.c. human tumors resulted in specific growth inhibition of PAX5-expressing tumors. This knowledge can be used for the therapeutic generation of CTL lines or the cloning of high-avidity T-cell receptor genes for use in adoptive immunotherapy.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Cell Proliferation
  • Chemotaxis, Leukocyte / immunology
  • Complement C5 / genetics
  • Genes, RAG-1 / physiology
  • Humans
  • Immunity, Cellular / physiology
  • Immunotherapy, Adoptive* / methods
  • Interleukin Receptor Common gamma Subunit / genetics
  • K562 Cells
  • Mice
  • Mice, Knockout
  • Neoplasms / immunology*
  • Neoplasms / metabolism
  • Neoplasms / pathology
  • Neoplasms / therapy*
  • PAX5 Transcription Factor / antagonists & inhibitors*
  • PAX5 Transcription Factor / immunology*
  • PAX5 Transcription Factor / metabolism
  • T-Lymphocytes / immunology
  • T-Lymphocytes / transplantation
  • Tumor Cells, Cultured
  • Xenograft Model Antitumor Assays

Substances

  • Complement C5
  • Interleukin Receptor Common gamma Subunit
  • PAX5 Transcription Factor
  • PAX5 protein, human