Gene Therapy Fulfilling Its Promise

N Engl J Med. 2009 Jan 29;360(5):518-21. doi: 10.1056/NEJMe0809614.

Publication types

  • Comment
  • Editorial
  • Historical Article

MeSH terms

  • Adenosine Deaminase / deficiency
  • Adenosine Deaminase / genetics
  • Child, Preschool
  • Genetic Therapy* / adverse effects
  • Genetic Therapy* / history
  • Genetic Vectors
  • Hematopoietic Stem Cell Transplantation*
  • Hematopoietic Stem Cells
  • History, 20th Century
  • History, 21st Century
  • Humans
  • Lymphocyte Count
  • Severe Combined Immunodeficiency / therapy*
  • T-Lymphocytes
  • X-Linked Combined Immunodeficiency Diseases / genetics
  • X-Linked Combined Immunodeficiency Diseases / therapy*

Substances

  • Adenosine Deaminase