Mutation L437P in the 2B domain of keratin 1 causes diffuse palmoplantar keratoderma in a Chinese pedigree

J Eur Acad Dermatol Venereol. 2009 Sep;23(9):1079-82. doi: 10.1111/j.1468-3083.2009.03175.x. Epub 2009 Mar 17.

Abstract

Diffuse palmoplantar keratoderma (DPPK) is an autosomal dominant genodermatosis characterized by uniform hyperkeratosis of the palm and sole epidermis. This disorder can be caused by mutations in the genes keratin 1, keratin 9, keratin 16, desmoglein 1 and plakoglobin. Here we present a DPPK Chinese pedigree and identify the aetiology as a novel missense mutation, L437P, located in a highly conserved helix motif in domain 2B of KRT1. Functional analysis shows that overexpression of the L437P mutant in cultured cells leads to abnormal intermediate filament networks and filament aggregation. This gain-of-function mutation highlights the role of domain 2B in mediating filament assembly.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • China
  • Female
  • Genetic Predisposition to Disease / ethnology
  • Genetic Predisposition to Disease / genetics
  • Genotype
  • Humans
  • Intermediate Filaments / pathology
  • Keratin-1 / genetics*
  • Keratoderma, Palmoplantar, Diffuse / ethnology*
  • Keratoderma, Palmoplantar, Diffuse / genetics*
  • Keratoderma, Palmoplantar, Diffuse / pathology
  • Male
  • Mutation, Missense / genetics*
  • Pedigree*
  • Phenotype

Substances

  • Keratin-1