Why did tarenflurbil fail in Alzheimer's disease?

J Alzheimers Dis. 2009;17(4):757-60. doi: 10.3233/JAD-2009-1092.

Abstract

There has been a lot of disappointment surrounding the recent failure of the largest ever study in patients with Alzheimer's disease (AD) with tarenflurbil, a compound believed to modulate the activity of gamma-secretase, the pivotal enzyme that generates the amyloid-beta (A beta) peptide from the amyloid-beta protein precursor. What are the reasons for this setback after the previous apparently encouraging results in a Phase II study? A straightforward explanation of this failure is that the gamma-secretase is not the right target for therapy or that, in general, blocking A beta does not produce clinical benefits in AD. If one still accepts a physiopathological role of A beta in AD, tarenflurbil could not be the right compound because of its weak pharmacological activity as an A beta(1-42) lowering agent and its poor brain penetration. In addition, based on previous negative results with several anti-inflammatory drugs in AD, it is hypothesized that the residual anti-inflammatory activity of tarenflurbil may have a detrimental effect on disease progression.

MeSH terms

  • Aged
  • Aged, 80 and over
  • Alzheimer Disease / drug therapy*
  • Alzheimer Disease / metabolism
  • Amyloid Precursor Protein Secretases / administration & dosage*
  • Amyloid Precursor Protein Secretases / adverse effects
  • Amyloid beta-Peptides / metabolism
  • Amyloid beta-Protein Precursor / metabolism
  • Brain / drug effects*
  • Brain / metabolism
  • Flurbiprofen / administration & dosage*
  • Flurbiprofen / adverse effects
  • Humans
  • Treatment Failure

Substances

  • Amyloid beta-Peptides
  • Amyloid beta-Protein Precursor
  • tarenflurbil
  • Flurbiprofen
  • Amyloid Precursor Protein Secretases