Less is more: therapeutic exon skipping for Duchenne muscular dystrophy

Lancet Neurol. 2009 Oct;8(10):873-5. doi: 10.1016/S1474-4422(09)70229-7. Epub 2009 Aug 25.
No abstract available

Publication types

  • Comment
  • Letter

MeSH terms

  • Animals
  • Dystrophin / genetics
  • Exons
  • Genetic Therapy / methods*
  • Humans
  • Mice
  • Muscular Dystrophy, Duchenne / genetics*
  • Muscular Dystrophy, Duchenne / therapy*
  • Oligonucleotides, Antisense / therapeutic use*

Substances

  • DMD protein, human
  • Dystrophin
  • Oligonucleotides, Antisense