Current enzyme replacement therapy for the treatment of lysosomal storage diseases

Pediatr Ann. 2009 Aug;38(8):448-55. doi: 10.3928/00904481-20090723-09.
No abstract available

Publication types

  • Review

MeSH terms

  • Enzyme Therapy*
  • Fabry Disease / drug therapy
  • Gaucher Disease / drug therapy
  • Glucosylceramidase / therapeutic use
  • Glycogen Storage Disease Type II / drug therapy
  • Humans
  • Infusions, Intravenous
  • Isoenzymes / therapeutic use
  • Lysosomal Storage Diseases, Nervous System / diagnosis
  • Lysosomal Storage Diseases, Nervous System / drug therapy*
  • Mucopolysaccharidoses / drug therapy
  • N-Acetylgalactosamine-4-Sulfatase / therapeutic use
  • Recombinant Proteins / administration & dosage
  • Recombinant Proteins / therapeutic use
  • alpha-Galactosidase / therapeutic use

Substances

  • Isoenzymes
  • Recombinant Proteins
  • N-Acetylgalactosamine-4-Sulfatase
  • galsulfase
  • alpha-Galactosidase
  • Glucosylceramidase
  • imiglucerase
  • agalsidase beta