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Comment
. 2009 Nov 6;326(5954):805-6.
doi: 10.1126/science.1181937.

Medicine. A comeback for gene therapy

Luigi Naldini  1
Affiliations
Comment

Medicine. A comeback for gene therapy

Luigi Naldini. Science. .
No abstract available

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  • Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy.
    Cartier N, Hacein-Bey-Abina S, Bartholomae CC, Veres G, Schmidt M, Kutschera I, Vidaud M, Abel U, Dal-Cortivo L, Caccavelli L, Mahlaoui N, Kiermer V, Mittelstaedt D, Bellesme C, Lahlou N, Lefrère F, Blanche S, Audit M, Payen E, Leboulch P, l'Homme B, Bougnères P, Von Kalle C, Fischer A, Cavazzana-Calvo M, Aubourg P. Cartier N, et al. Science. 2009 Nov 6;326(5954):818-23. doi: 10.1126/science.1171242. Science. 2009. PMID: 19892975

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