Similar articles

• Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia.

  Cavazzana-Calvo M, Payen E, Negre O, Wang G, Hehir K, Fusil F, Down J, Denaro M, Brady T, Westerman K, Cavallesco R, Gillet-Legrand B, Caccavelli L, Sgarra R, Maouche-Chrétien L, Bernaudin F, Girot R, Dorazio R, Mulder GJ, Polack A, Bank A, Soulier J, Larghero J, Kabbara N, Dalle B, Gourmel B, Socie G, Chrétien S, Cartier N, Aubourg P, Fischer A, Cornetta K, Galacteros F, Beuzard Y, Gluckman E, Bushman F, Hacein-Bey-Abina S, Leboulch P. Cavazzana-Calvo M, et al. Nature. 2010 Sep 16;467(7313):318-22. doi: 10.1038/nature09328. Nature. 2010. PMID: 20844535 Free PMC article.
• Gene therapy. Beta-thalassemia treatment succeeds, with a caveat.

  Kaiser J. Kaiser J. Science. 2009 Dec 11;326(5959):1468-9. doi: 10.1126/science.326.5959.1468-b. Science. 2009. PMID: 20007873 No abstract available.
• Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia.

  Ronen K, Negre O, Roth S, Colomb C, Malani N, Denaro M, Brady T, Fusil F, Gillet-Legrand B, Hehir K, Beuzard Y, Leboulch P, Down JD, Payen E, Bushman FD. Ronen K, et al. Mol Ther. 2011 Jul;19(7):1273-86. doi: 10.1038/mt.2011.20. Epub 2011 Mar 8. Mol Ther. 2011. PMID: 21386821 Free PMC article.
• Hemoglobin gene therapy for β-thalassemia.

  Bank A. Bank A. Hematol Oncol Clin North Am. 2010 Dec;24(6):1187-201. doi: 10.1016/j.hoc.2010.08.002. Hematol Oncol Clin North Am. 2010. PMID: 21075288 Review.
• Recent Progress on Genetic Diagnosis and Therapy for β-Thalassemia in China and Around the World.

  Zhang J, Yan J, Zeng F. Zhang J, et al. Hum Gene Ther. 2018 Feb;29(2):197-203. doi: 10.1089/hum.2017.228. Hum Gene Ther. 2018. PMID: 29357712 Review.