No abstract available
MeSH terms
-
Adolescent
-
Adult
-
Carrier Proteins
-
Child
-
Clinical Trials as Topic
-
Eye Proteins
-
Genetic Therapy / methods*
-
Genetic Therapy / trends
-
Genetic Vectors
-
Humans
-
Leber Congenital Amaurosis / genetics
-
Leber Congenital Amaurosis / therapy*
-
Retinal Diseases / therapy*
-
Treatment Outcome
-
Visual Acuity
-
cis-trans-Isomerases
Substances
-
Carrier Proteins
-
Eye Proteins
-
retinoid isomerohydrolase
-
cis-trans-Isomerases