The risks of therapeutic misconception and individual patient (n=1) "trials" in rare diseases such as Duchenne dystrophy

Neuromuscul Disord. 2011 Jan;21(1):13-5. doi: 10.1016/j.nmd.2010.09.012. Epub 2010 Nov 3.
No abstract available

MeSH terms

  • Clinical Trials as Topic
  • Humans
  • Muscular Dystrophy, Duchenne / therapy*
  • Precision Medicine / methods*
  • Therapeutic Misconception*