Blind dogs that can see: pharmacological treatment of Leber congenital amaurosis caused by a defective visual cycle

Arch Ophthalmol. 2010 Nov;128(11):1483-5. doi: 10.1001/archophthalmol.2010.245.
No abstract available

Publication types

  • Editorial
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Comment

MeSH terms

  • Animals
  • Disease Models, Animal*
  • Diterpenes
  • Dogs
  • Electroretinography
  • Eye Proteins / genetics
  • Intravitreal Injections
  • Leber Congenital Amaurosis / drug therapy*
  • Leber Congenital Amaurosis / genetics
  • Leber Congenital Amaurosis / physiopathology
  • Mutation
  • Retinaldehyde / administration & dosage*
  • Vision, Ocular / physiology*
  • Visual Acuity / physiology

Substances

  • Diterpenes
  • Eye Proteins
  • 9-cis-retinal
  • Retinaldehyde