Editorial
doi: 10.1056/NEJMe1010123.
Targeting the basic defect in cystic fibrosis
- PMID: 21083391
- DOI: 10.1056/NEJMe1010123
Item in Clipboard
Editorial
Targeting the basic defect in cystic fibrosis
N Engl J Med.
.
No abstract available
Comment on
-
Effect of VX-770 in persons with cystic fibrosis and the G551D-CFTR mutation.N Engl J Med. 2010 Nov 18;363(21):1991-2003. doi: 10.1056/NEJMoa0909825. N Engl J Med. 2010. PMID: 21083385 Free PMC article. Clinical Trial.
Similar articles
-
Potentiators for cystic fibrosis - targeting the underlying molecular defect.Paediatr Respir Rev. 2015 Jun;16(3):162-4. doi: 10.1016/j.prrv.2015.04.003. Epub 2015 Apr 20. Paediatr Respir Rev. 2015. PMID: 26002404 Review. No abstract available.
-
Cystic fibrosis transmembrane conductance regulator biomarkers in 'real life': can we evaluate individual efficacy of cystic fibrosis transmembrane conductance regulator therapy?Ther Adv Respir Dis. 2015 Aug;9(4):198-200. doi: 10.1177/1753465815579364. Ther Adv Respir Dis. 2015. PMID: 26175480 No abstract available.
-
Ivacaftor in a G551D homozygote with cystic fibrosis.N Engl J Med. 2013 Sep 26;369(13):1280-2. doi: 10.1056/NEJMc1213681. N Engl J Med. 2013. PMID: 24066763 No abstract available.
-
Excitement mounts for first disease-modifying cystic fibrosis drugs.Nat Rev Drug Discov. 2011 Jul 1;10(7):479-80. doi: 10.1038/nrd3488. Nat Rev Drug Discov. 2011. PMID: 21720393 No abstract available.
-
Newborn screening for cystic fibrosis: Is there benefit for everyone?Paediatr Respir Rev. 2019 Aug;31:3-5. doi: 10.1016/j.prrv.2019.02.003. Epub 2019 Feb 28. Paediatr Respir Rev. 2019. PMID: 30956155 Review.
Cited by
-
Ivacaftor: a novel mutation modulating drug.J Clin Diagn Res. 2014 Nov;8(11):SE01-5. doi: 10.7860/JCDR/2014/6486.5158. Epub 2014 Nov 20. J Clin Diagn Res. 2014. PMID: 25584290 Free PMC article. Review.
-
Requirements for ion and solute transport, and pH regulation during enamel maturation.J Cell Physiol. 2012 Apr;227(4):1776-85. doi: 10.1002/jcp.22911. J Cell Physiol. 2012. PMID: 21732355 Free PMC article.
Publication types
MeSH terms
Substances
LinkOut - more resources
Full Text Sources
Medical
