Gene down-regulation with short hairpin RNAs and validation of specificity by inducible rescue in mammalian cells

Curr Protoc Cell Biol. 2010 Dec:Chapter 27:Unit 27.2. doi: 10.1002/0471143030.cb2702s49.

Abstract

The principal problem with RNA interference (RNAi) experiments is off-target effects. The most vigorous demonstration of the specificity is the rescue of the RNAi effects with an RNAi-resistant target gene. By combining the expression of short hairpin RNA (shRNA) and rescue cDNA in the same vector, both the validation of shRNA specificity and the generation of shRNA-expressing cell lines can easily be accomplished. If the compensatory cDNA is under the control of an inducible promoter, stable shRNA-expressing cells can be generated before the knockdown phenotypes are studied, by conditionally turning off the rescue protein. The use of model systems is detailed in these protocols.

MeSH terms

  • Animals
  • Cell Line
  • Down-Regulation*
  • Gene Knockdown Techniques / methods*
  • Genetic Vectors / genetics
  • Genetic Vectors / metabolism
  • Humans
  • Inverted Repeat Sequences*
  • Mammals / genetics*
  • Mammals / metabolism
  • RNA Interference
  • RNA, Small Interfering / genetics*
  • RNA, Small Interfering / metabolism
  • Species Specificity

Substances

  • RNA, Small Interfering