Therapy for cystic fibrosis--the end of the beginning?
- PMID: 22047565
- DOI: 10.1056/NEJMe1110323
Therapy for cystic fibrosis--the end of the beginning?
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A CFTR potentiator in patients with cystic fibrosis and the G551D mutation.N Engl J Med. 2011 Nov 3;365(18):1663-72. doi: 10.1056/NEJMoa1105185. N Engl J Med. 2011. PMID: 22047557 Free PMC article. Clinical Trial.
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