Clinical progress in gene therapy: sustained partial correction of the bleeding disorder in patients suffering from severe hemophilia B

Hum Gene Ther. 2012 Jan;23(1):4-6. doi: 10.1089/hum.2011.221.
No abstract available

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Clinical Trials as Topic
  • Dependovirus / immunology
  • Dependovirus / metabolism
  • Factor IX / immunology
  • Factor IX / metabolism
  • Factor VIII / immunology
  • Factor VIII / metabolism
  • Genetic Therapy*
  • Genetic Vectors / immunology
  • Genetic Vectors / metabolism
  • Hemophilia A / immunology
  • Hemophilia A / metabolism
  • Hemophilia A / pathology
  • Hemophilia A / therapy
  • Hemophilia B / immunology
  • Hemophilia B / metabolism
  • Hemophilia B / pathology
  • Hemophilia B / therapy*
  • Hemorrhage / immunology
  • Hemorrhage / metabolism
  • Hemorrhage / pathology
  • Hemorrhage / therapy*
  • Hepatocytes / immunology
  • Hepatocytes / metabolism
  • Humans
  • Liver / immunology
  • Liver / metabolism

Substances

  • Factor VIII
  • Factor IX