Challenges in vector and trial design using retroviral vectors for long-term gene correction in hematopoietic stem cell gene therapy

Mol Ther. 2012 Jun;20(6):1084-94. doi: 10.1038/mt.2012.93.
No abstract available

Publication types

  • Congress
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Gene Transfer Techniques
  • Genetic Therapy* / adverse effects
  • Genetic Therapy* / ethics
  • Genetic Therapy* / legislation & jurisprudence
  • Genetic Vectors* / adverse effects
  • Genetic Vectors* / genetics
  • Hematopoietic Stem Cell Transplantation*
  • Humans
  • Research Design
  • Retroviridae / genetics*