A randomised, double-blind, sham-controlled study of granulocyte/monocyte apheresis for moderate to severe Crohn's disease

Gut. 2013 Sep;62(9):1288-94. doi: 10.1136/gutjnl-2011-300995. Epub 2012 Jul 3.

Abstract

Objectives: Activated granulocytes and monocytes may contribute to the pathogenesis of Crohn's disease (CD). In small, uncontrolled studies, granulocyte/monocyte apheresis (GMA) has shown promise in treating CD. We conducted a randomised, double-blind study to compare GMA with a sham procedure in patients with moderate to severe CD.

Design: Patients with active CD as defined by a Crohn's Disease Activity Index (CDAI) of 220-450 were randomly allocated in a 2:1 ratio to treatment with GMA using the Adacolumn Apheresis System (JIMRO, Takasaki, Japan) or sham apheresis. Ten apheresis sessions were scheduled over a 9-week period, and efficacy was evaluated at week 12. The primary end point was the proportion of patients achieving clinical remission (CDAI score ≤ 150 without use of prohibited drugs).

Results: Clinical remission was achieved by 17.8% of patients in the GMA group (n = 157) compared with 19.2% of those in the sham control group (n = 78) (absolute difference--1.4% (95% CI--12.8% to 8.5%), p = 0.858). Clinical response (defined as a ≥ 100-point decrease in CDAI) was achieved by 28.0% and 26.9% of patients in the GMA and sham groups, respectively (p = 1.000). The two treatments produced similar changes from baseline in CDAI and quality of life, as well as in disease severity assessed endoscopically. The incidence and types of adverse events did not differ between groups.

Conclusions: GMA was well tolerated, but this study did not demonstrate its effectiveness over a sham procedure in inducing clinical remission or response in patients with moderate to severe CD.

Trial registration: ClinicalTrials.gov NCT00162942.

Keywords: Blood component removal; granulocytes; inflammatory bowel disease; monocytes; remission induction.

Publication types

  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Blood Component Removal* / adverse effects
  • Blood Component Removal* / methods
  • Crohn Disease / diagnosis
  • Crohn Disease / immunology
  • Crohn Disease / physiopathology
  • Crohn Disease / psychology
  • Crohn Disease / therapy*
  • Double-Blind Method
  • Endoscopy, Gastrointestinal / methods
  • Female
  • Granulocytes / immunology*
  • Humans
  • Male
  • Middle Aged
  • Monocytes / immunology*
  • Placebos
  • Quality of Life
  • Remission Induction / methods
  • Severity of Illness Index
  • Treatment Outcome

Substances

  • Placebos

Associated data

  • ClinicalTrials.gov/NCT00162942