No abstract available
MeSH terms
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Clinical Trials as Topic*
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Drug Industry
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Gene Dosage
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Genome, Human
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Heterozygote
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Histone Deacetylase Inhibitors / therapeutic use
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Histone Deacetylases / administration & dosage
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Humans
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Infant, Newborn
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Molecular Targeted Therapy
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Motor Neurons / drug effects
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Motor Neurons / metabolism*
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Muscular Atrophy, Spinal / drug therapy*
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Mutation
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Survival of Motor Neuron 1 Protein / genetics*
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Survival of Motor Neuron 1 Protein / therapeutic use
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Survival of Motor Neuron 2 Protein / genetics
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Survival of Motor Neuron 2 Protein / therapeutic use
Substances
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Histone Deacetylase Inhibitors
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SMN1 protein, human
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SMN2 protein, human
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Survival of Motor Neuron 1 Protein
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Survival of Motor Neuron 2 Protein
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Histone Deacetylases