Clinical trial preparedness in facioscapulohumeral dystrophy: outcome measures and patient access: 8-9 April 2013, Leiden, The Netherlands

Neuromuscul Disord. 2014 Jan;24(1):79-85. doi: 10.1016/j.nmd.2013.07.009. Epub 2013 Aug 2.

Authors

R Tawil¹, D W Shaw², S M van der Maarel³, S J Tapscott⁴

Affiliations

¹ Department of Neurology, University of Rochester Medical Center, Rochester, NY, United States. Electronic address: rabi_tawil@URMC.rochester.edu.
² Department of Radiology, Seattle Children's Hospital, Seattle, WA, United States.
³ Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands.
⁴ Division of Human Biology, Fred Hutchinson Cancer Research Center, Seattle, WA, United States.

PMID: 24011701
DOI: 10.1016/j.nmd.2013.07.009

No abstract available

Publication types

Consensus Development Conference

MeSH terms

Biomarkers / analysis
Clinical Trials as Topic
Humans
Muscular Dystrophy, Facioscapulohumeral / therapy*
Registries
Treatment Outcome

Substances

Biomarkers