Design, optimization, and biological evaluation of novel keto-benzimidazoles as potent and selective inhibitors of phosphodiesterase 10A (PDE10A)

J Med Chem. 2013 Nov 14;56(21):8781-92. doi: 10.1021/jm401234w. Epub 2013 Oct 25.

Abstract

Our development of PDE10A inhibitors began with an HTS screening hit (1) that exhibited both high p-glycoprotein (P-gp) efflux ratios in rat and human and poor metabolic stability. On the basis of cocrystal structure of 1 in human PDE10A enzyme, we designed a novel keto-benzimidazole 26 with comparable PDE10A potency devoid of efflux liabilities. On target in vivo coverage of PDE10A in rat brain was assessed using our previously reported LC-MS/MS receptor occupancy (RO) technology. Compound 26 achieved 55% RO of PDE10A at 30 mg/kg po and covered PDE10A receptors in rat brain in a dose-dependent manner. Cocrystal structure of 26 in PDE10A confirmed the binding mode of the novel scaffold. Further optimization resulted in the identification of keto-benzimidazole 34, which showed an increased in vivo efficacy of 57% RO in rats at 10 mg/kg po and an improved in vivo rat clearance and oral bioavailability.

MeSH terms

  • Animals
  • Benzimidazoles / administration & dosage
  • Benzimidazoles / chemical synthesis
  • Benzimidazoles / pharmacology*
  • Cells, Cultured
  • Dose-Response Relationship, Drug
  • Drug Design*
  • Humans
  • Ketones / administration & dosage
  • Ketones / chemical synthesis
  • Ketones / pharmacology*
  • Male
  • Models, Molecular
  • Molecular Structure
  • Phosphodiesterase Inhibitors / administration & dosage
  • Phosphodiesterase Inhibitors / chemical synthesis
  • Phosphodiesterase Inhibitors / pharmacology*
  • Phosphoric Diester Hydrolases / metabolism*
  • Rats
  • Rats, Sprague-Dawley
  • Structure-Activity Relationship
  • Swine

Substances

  • Benzimidazoles
  • Ketones
  • Phosphodiesterase Inhibitors
  • PDE10A protein, human
  • Phosphoric Diester Hydrolases

Associated data

  • PDB/4MUW
  • PDB/4MVH