Antisense-mediated exon skipping: networking to meet opportunities and to overcome challenges

Nucleic Acid Ther. 2014 Feb;24(1):1-3. doi: 10.1089/nat.2014.1500.
No abstract available

Publication types

  • Editorial
  • Introductory Journal Article

MeSH terms

  • Cooperative Behavior
  • Exons*
  • Humans
  • Male
  • Muscular Dystrophy, Duchenne / genetics
  • Muscular Dystrophy, Duchenne / therapy
  • Oligonucleotides, Antisense / genetics*
  • Oligonucleotides, Antisense / therapeutic use*
  • Rare Diseases / genetics
  • Rare Diseases / therapy
  • Targeted Gene Repair

Substances

  • Oligonucleotides, Antisense