Phase I/II ex vivo gene therapy clinical trial for recessive dystrophic epidermolysis bullosa using skin equivalent grafts genetically corrected with a COL7A1-encoding SIN retroviral vector (GENEGRAFT)

Hum Gene Ther Clin Dev. 2014 Jun;25(2):65-6. doi: 10.1089/humc.2014.2508.
No abstract available

MeSH terms

  • Clinical Trials as Topic
  • Collagen Type VII / genetics*
  • Collagen Type VII / metabolism
  • Epidermolysis Bullosa Dystrophica / therapy*
  • Fibroblasts / cytology
  • Fibroblasts / metabolism
  • Fibroblasts / transplantation
  • Genetic Therapy
  • Genetic Vectors / genetics
  • Genetic Vectors / metabolism*
  • Humans
  • Keratinocytes / cytology
  • Keratinocytes / metabolism
  • Keratinocytes / transplantation
  • Retroviridae / genetics*

Substances

  • Collagen Type VII