Successful RAG1-SCID Gene Therapy Depends on the Level of RAG1 Expression

J Allergy Clin Immunol. 2014 Jul;134(1):242-3. doi: 10.1016/j.jaci.2014.04.033. Epub 2014 Jun 26.

Publication types

  • Letter
  • Comment

MeSH terms

  • Animals
  • Female
  • Genetic Therapy*
  • Genetic Vectors / genetics*
  • Homeodomain Proteins / genetics*
  • Humans
  • Lentivirus / genetics*
  • Male
  • Severe Combined Immunodeficiency / genetics*
  • Severe Combined Immunodeficiency / therapy*

Substances

  • Homeodomain Proteins