Rare inherited diseases merit disease-specific trials

Lancet Neurol. 2015 Oct;14(10):968-9. doi: 10.1016/S1474-4422(15)00217-3. Epub 2015 Aug 25.

Author

Alexandra Durr¹

Affiliation

¹ APHP, Department of Genetics, Inserm U 1127, CNRS UMR 7225, Sorbonne Universités, UPMC Univ Paris 06 UMR S 1127, Institut du Cerveau et de la Moelle Épinière, ICM, University Hospital Pitié-Salpêtrière, Paris, France. Electronic address: alexandra.durr@upmc.fr.

PMID: 26321319
DOI: 10.1016/S1474-4422(15)00217-3

No abstract available

Publication types

Comment

MeSH terms

Excitatory Amino Acid Antagonists / pharmacology*
Female
Friedreich Ataxia / drug therapy*
Humans
Male
Riluzole / pharmacology*
Spinocerebellar Ataxias / drug therapy*

Substances

Excitatory Amino Acid Antagonists
Riluzole