MTHFD1 formyltetrahydrofolate synthetase deficiency, a model for the MTHFD1 R653Q variant, leads to congenital heart defects in mice

Birth Defects Res A Clin Mol Teratol. 2015 Dec;103(12):1031-8. doi: 10.1002/bdra.23451. Epub 2015 Sep 26.

Abstract

Background: A single nucleotide polymorphism (SNP) in the synthetase domain of the trifunctional folate-dependent enzyme MTHFD1 (c.1958G>A, R653Q) has been linked to adverse pregnancy outcomes, neural tube defects, and possibly congenital heart defects. Maternal folate deficiency may also modify the risk associated with these disorders. We recently established a mouse model with a mild deficiency of 10-formyltetrahydrofolate synthetase activity in MTHFD1 (Mthfd1S(+/-) mice) to investigate disorders associated with SNPs in this gene. The effect of synthetase deficiency on embryonic heart development has not yet been examined.

Methods: Female Mthfd1S(+/+) and (+/-) mice were placed on control and folate-deficient diets for 6 weeks before mating to Mthfd1S(+/-) males. Embryos and placentae were collected at embryonic day 14.5. Embryos were evaluated for congenital heart defects by histological examination.

Results: Embryonic Mthfd1S(+/-) genotype was associated with an increased incidence of heart defects, primarily ventricular septal defects. Other markers of embryonic development (crown-rump length, embryonic weight, embryonic delay, placental weight, and thickness of the ventricular myocardium) were not affected by embryonic genotype. Maternal genotype and diet did not have a significant effect on these outcomes.

Conclusion: Deficiency of the MTHFD1 10-formyltetrahydrofolate synthetase activity in embryos is associated with increased incidence of congenital heart defects.

Keywords: 10-formyltetrahydrofolate synthetase; MTHFD1; congenital heart defects; folic acid; one-carbon folate metabolism; rs2236225; ventricular septal defect.

MeSH terms

  • Aminohydrolases / genetics*
  • Animals
  • Disease Models, Animal*
  • Female
  • Formate-Tetrahydrofolate Ligase / genetics*
  • Heart Defects, Congenital / genetics*
  • Male
  • Methylenetetrahydrofolate Dehydrogenase (NADP) / genetics*
  • Mice
  • Mice, Inbred BALB C
  • Mice, Knockout
  • Multienzyme Complexes / genetics*

Substances

  • Multienzyme Complexes
  • formyl-methenyl-methylenetetrahydrofolate synthetase
  • Methylenetetrahydrofolate Dehydrogenase (NADP)
  • Aminohydrolases
  • Formate-Tetrahydrofolate Ligase