Moving toward a gene therapy for Huntington's disease

Gene Ther. 2015 Dec;22(12):931-3. doi: 10.1038/gt.2015.102.

Authors

J C Glorioso¹, J B Cohen¹, D L Carlisle², I Munoz-Sanjuan³, R M Friedlander²

Affiliations

¹ Department of Microbiology and Molecular Genetics, The University of Pittsburgh School of Medicine, Pittsburgh, PA, USA.
² Department of Neurological Surgery, The University of Pittsburgh School of Medicine, Pittsburgh, PA, USA.
³ CHDI Foundation/CHDI Management, Los Angeles, CA, USA. E-mail: glorioso@pitt.edu.

PMID: 26633828
DOI: 10.1038/gt.2015.102

No abstract available

Publication types

Editorial

MeSH terms

Animals
Disease Models, Animal
Genetic Therapy / methods*
Humans
Huntington Disease / genetics*
Huntington Disease / metabolism
Huntington Disease / therapy*
Mice
Peptides / genetics
Peptides / metabolism

Substances

Peptides
polyglutamine