Gene Therapy for Hemoglobinopathies: Tremendous Successes and Remaining Caveats
Mol Ther
.
2016 Apr;24(4):668-70.
doi: 10.1038/mt.2016.57.
Author
Punam Malik
1
Affiliation
1
Division of Experimental Hematology and Cancer Biology, Cancer and Blood Diseases Institute, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
PMID:
27081721
PMCID:
PMC4886952
DOI:
10.1038/mt.2016.57
No abstract available
MeSH terms
Animals
Clinical Trials as Topic
Disease Models, Animal
Genetic Therapy / methods*
Genetic Vectors / genetics
Hemoglobinopathies / therapy*
Humans
Lentivirus / genetics