The CRISPR Way to Think about Duchenne's
- PMID: 27119241
- DOI: 10.1056/NEJMcibr1601383
The CRISPR Way to Think about Duchenne's
Similar articles
-
Dystrophin immunity in Duchenne's muscular dystrophy.N Engl J Med. 2010 Oct 7;363(15):1429-37. doi: 10.1056/NEJMoa1000228. N Engl J Med. 2010. PMID: 20925545 Free PMC article. Clinical Trial.
-
Adenoviral vectors encoding CRISPR/Cas9 multiplexes rescue dystrophin synthesis in unselected populations of DMD muscle cells.Sci Rep. 2016 Nov 15;6:37051. doi: 10.1038/srep37051. Sci Rep. 2016. PMID: 27845387 Free PMC article.
-
Neuromuscular disease: CRISPR/Cas9 gene-editing platform corrects mutations associated with Duchenne muscular dystrophy.Nat Rev Neurol. 2015 Apr;11(4):184. doi: 10.1038/nrneurol.2015.37. Epub 2015 Mar 10. Nat Rev Neurol. 2015. PMID: 25752950 No abstract available.
-
Harnessing the potential of dystrophin-related proteins for ameliorating Duchenne's muscular dystrophy.Acta Physiol Scand. 2001 Mar;171(3):349-58. doi: 10.1046/j.1365-201x.2001.00838.x. Acta Physiol Scand. 2001. PMID: 11412148 Review.
-
The future of Duchenne muscular dystrophy gene therapy: shrinking the dystrophin gene.Curr Opin Mol Ther. 2002 Aug;4(4):343-8. Curr Opin Mol Ther. 2002. PMID: 12222872 Review.
Cited by
-
Human iPSC model reveals a central role for NOX4 and oxidative stress in Duchenne cardiomyopathy.Stem Cell Reports. 2022 Feb 8;17(2):352-368. doi: 10.1016/j.stemcr.2021.12.019. Epub 2022 Jan 27. Stem Cell Reports. 2022. PMID: 35090586 Free PMC article.
-
Plasmid-Mediated Gene Therapy in Mouse Models of Limb Girdle Muscular Dystrophy.Mol Ther Methods Clin Dev. 2019 Oct 14;15:294-304. doi: 10.1016/j.omtm.2019.10.002. eCollection 2019 Dec 13. Mol Ther Methods Clin Dev. 2019. PMID: 31890729 Free PMC article.
-
Gene Editing and Gene-Based Therapeutics for Cardiomyopathies.Heart Fail Clin. 2018 Apr;14(2):179-188. doi: 10.1016/j.hfc.2017.12.006. Heart Fail Clin. 2018. PMID: 29525646 Free PMC article. Review.
-
Recent developments in Duchenne muscular dystrophy: facts and numbers.J Cachexia Sarcopenia Muscle. 2017 Oct;8(5):681-685. doi: 10.1002/jcsm.12245. J Cachexia Sarcopenia Muscle. 2017. PMID: 29076660 Free PMC article. No abstract available.
-
Myopenia and precision (P4) medicine.J Cachexia Sarcopenia Muscle. 2017 Dec;8(6):857-863. doi: 10.1002/jcsm.12231. Epub 2017 Sep 24. J Cachexia Sarcopenia Muscle. 2017. PMID: 28944582 Free PMC article.
MeSH terms
Substances
LinkOut - more resources
Full Text Sources
Other Literature Sources