Clinical Trial of Erythropoietin in Young Children With Cerebral Palsy

J Child Neurol. 2016 Sep;31(10):1227-34. doi: 10.1177/0883073816650038. Epub 2016 May 27.

Abstract

This study was conducted to assess the safety and efficacy of recombinant human erythropoietin in young children with cerebral palsy aged between 6 months and 3 years. All participants received subcutaneous recombinant human erythropoietin and 8 weeks of rehabilitation therapy. Adverse events, changes of vital signs, and hematologic tests were monitored up to 8 weeks postinjection. Functional measures of development at 4 and 8 weeks postinjection were compared with baseline values, and improvements were compared with those of an age-matched historical control group. Nine participants completed the trial from June 2012 to February 2015. No adverse events were related to recombinant human erythropoietin. Erythropoiesis was noted, although within normal range. Functional improvements were observed in all participants (P < .05) and increases in motor function were higher in recombinant human erythropoietin group than the control group. Accordingly, recombinant human erythropoietin administration was safe without any significant adverse events and improved the functional outcomes in young children with cerebral palsy.

Keywords: cerebral palsy; efficacy; erythropoietin; safety; therapy.

Publication types

  • Clinical Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cerebral Palsy / drug therapy*
  • Cerebral Palsy / rehabilitation
  • Child, Preschool
  • Erythropoietin / adverse effects
  • Erythropoietin / therapeutic use*
  • Female
  • Humans
  • Infant
  • Injections, Subcutaneous
  • Male
  • Neuromuscular Agents / adverse effects
  • Neuromuscular Agents / therapeutic use*
  • Recombinant Proteins / adverse effects
  • Recombinant Proteins / therapeutic use
  • Treatment Outcome

Substances

  • EPO protein, human
  • Neuromuscular Agents
  • Recombinant Proteins
  • Erythropoietin