Why we should care about ultra-rare disease

Eur Respir Rev. 2016 Jun;25(140):101-3. doi: 10.1183/16000617.0017-2016.

Abstract

Orphan drugs for patients with ultra-rare diseases: between cost-effectiveness and equality of access to cure http://ow.ly/Zlmf4

Publication types

  • Editorial

MeSH terms

  • Drug Discovery / legislation & jurisprudence
  • Europe / epidemiology
  • Government Regulation
  • Health Policy / legislation & jurisprudence*
  • Health Services Accessibility / legislation & jurisprudence*
  • Humans
  • Lung Diseases / classification
  • Lung Diseases / diagnosis
  • Lung Diseases / drug therapy*
  • Lung Diseases / epidemiology
  • Orphan Drug Production / legislation & jurisprudence*
  • Rare Diseases / classification
  • Rare Diseases / diagnosis
  • Rare Diseases / drug therapy*
  • Rare Diseases / epidemiology